03/11/2025
Retinosis pigmentaria cura, otro gene modificador para varios genes ( gene-agnóstico). https://sparingvision.com/sparingvision-doses-first-patient-with-spvn20-for-advanced-retinitis-pigmentosa-in-nyrvana-trial/🥳
Favorable safety profile of SPVN06 observed in Phase I including nine patients with severe advanced retinitis pigmentosa. Trial advances into Phase II extension phase, with two highest doses of SPVN06, following DSMB positive recommendation