Human Gene and Cell Therapy Center

29/07/2025

🧬 NOW OPEN: Registration for Breakthroughs in Targeted In Vivo Gene Editing!

On Nov. 20-21, dive into cutting-edge solutions for targeted delivery of technology in vivo in San Diego + virtually. https://bit.ly/4lIckCG

13/02/2025

https://annualmeeting.asgct.org/register/patient-advocates?fbclid=IwY2xjawIajJZleHRuA2FlbQIxMAABHSsCujZyVHrNHG04ATpJioW1JhlkWr-16ts69euwze-_vZHFfzphBdi3Lw_aem_j2meWRwsiBmsPRN3-M9-YA

ASGCT recognizes the critical role patient advocacy organizations and foundations play in developing treatments and helping those with a disease or disorder navigate the complex journey of  gene and cell therapies.  ASGCT offers a limited number of complimentary registrations to support the abilit...

22/01/2025

Starting TOMORROW: ASGCT and FDA are hosting a free scientific workshop exploring immunogenicity challenges across AAV gene therapies!

Join leading researchers and regulators for discussions on immune responses, antibody testing methodologies, and redosing strategies in AAV development. Seven FDA OTP representatives will share regulatory perspectives alongside experts from UMass Chan Medical School, University of Florida, Sarepta Therapeutics, and other institutions.

January 22-23, 2025
9:00 AM - 1:00 PM ET
Virtual | Free
Register: www.asgct.org/2025aav

21/12/2024

Olezarsen@is the first approved treatment in the U.S. for FCS, which prevents the body from breaking down fats. The treatment is an@antisense oligonucleotide (A*O).

18/03/2024

https://www.science.org/content/article/breakthrough-of-the-year-2023

Blockbuster medicines targeting GLP-1 hormone also improve heart health in a large trial, show promise for wider range of conditions

15/03/2023

This summit is dedicated to actionable insights to optimise analytical development for gene therapy products.

15/03/2023

The European Commission gave conditional approval to Hemgenix, a infusion gene therapy for adults with hemophilia B and no inhibitors.

14/03/2023

The mRNA-Based Therapeutics Summit is the only meeting focused on the development of mRNA vaccines and therapies from early basic research through to commercialization and patients.

11/01/2023

Informa Connect's Next Generation CAR and T cell therapies event pioneers point of care with innovative manufacturing and commercialization strategies. Revolutionize cell engineering with ground breaking autologous and allogeneic treatments for blood borne and solid tumors.

27/12/2022

Ferring Receives Approval from U.S. FDA for Adstiladrin for High-Risk, BCG-Unresponsive Non-Muscle Invasive Bladder Cancer Ferring Receives Approval from U.S. FDA for Adstiladrin for High-Risk, BCG-Unresponsive Non-Muscle Invasive Bladder Cancer 16 December 2022 celia By celia 16 December 2022 0 Sha...