NS Pharma Inc.

02/20/2026

Dallas, we’re headed your way. 💙

We are excited to take part in the upcoming CureDuchenne Workshop and spend the day immersed in meaningful dialogue around Duchenne muscular dystrophy. These gatherings create space for real conversations about care, research, and the lived experiences of families navigating Duchenne.

We value the opportunity to be present, to learn, and to support a community that continues to inspire progress.

Learn more about the workshop: https://ow.ly/V9FX50YiHJv

02/18/2026

With approaching on 2/28, we want to thank the families who’ve allowed us to be a part of their Duchenne journey. Their stories remind us why awareness and education are essential.

Explore their Duchenne journeys: https://ow.ly/S7vL50Yhu5C

02/13/2026

What an incredible experience at WORLDSymposium 2026!

We were grateful to see well over 70 attendees join our session and take part in a meaningful conversation around MPS II. A special thank you to Drs. Hoffman, Burton, and Jalazo for delivering an outstanding presentation that provided a thoughtful overview of the disease, insights into the evolving paradigm of care, and powerful reflections drawn from personal and clinical experience.

The discussion and Q&A were so engaging that we had to bring the session to a close after running over our allotted time, which speaks to the level of interest and collaboration in the room.

Thank you to everyone who attended, asked questions, and helped make this such a memorable and impactful session. We look forward to continuing these important conversations.

02/11/2026

Today we celebrate International Day of Women and Girls in Science by recognizing the talented women at NS Pharma whose curiosity, dedication, and leadership help drive scientific progress.

Across research, development, clinical science, and patient focused roles, women in STEM play a critical role in advancing innovation and improving outcomes for people living with rare diseases. Their expertise, perspectives, and commitment shape our work and strengthen our teams every day.

We are proud to highlight and support the women in science at NS Pharma and to celebrate women and girls everywhere who are building a more inclusive future for discovery and progress.

02/09/2026

We are currently hiring a Patient Engagement Lead (PEL) to join our team and support individuals and families living with rare diseases.

This role is an opportunity to serve as a trusted resource for patients and caregivers, helping them navigate access to therapy, understand available support services, and feel supported throughout their treatment journey. The Patient Engagement Lead works closely with internal teams and patient advocacy partners, with a strong focus on conditions such as Duchenne muscular dystrophy and Hunter syndrome.

If you are passionate about patient support, have experience in specialty pharmacy or market access, and are motivated by making a meaningful difference in rare disease care, we invite you to learn more.

Explore the role and apply here:
https://ow.ly/nWOk50YbxYf

02/06/2026

We are looking forward to attending this upcoming event and connecting with members of the rare disease community.

Opportunities like this allow for meaningful dialogue, shared learning, and continued collaboration among patients, caregivers, healthcare professionals, and researchers. We value the chance to listen, learn, and engage in conversations that help move care and understanding forward.

Learn more about the event here https://ow.ly/RY9k50Y9Qx8

02/02/2026

Today, we are proud to be presenting at WORLDSymposium 2026.

This meeting plays an important role in bringing together the lysosomal disease community to share knowledge, foster collaboration, and advance scientific understanding. NS Pharma is honored to contribute to this exchange and to connect with others who share a commitment to progress in rare disease research and care.

Thank you to the organizers and attendees for creating a space that supports collaboration and learning.

01/30/2026

This is exciting progress for the Duchenne community.

Newborn screening has the power to change lives through earlier identification and earlier support for families. Adding Duchenne muscular dystrophy to the Recommended Uniform Screening Panel (RUSP) is a meaningful step toward more consistent screening and earlier care across states.

We’re encouraged to see continued education and resources that help move this important conversation forward and keep families at the center.

🆕 Introducing the Newborn Screening Resource Roadmap.

❓ Is the condition present in early childhood? Is it currently screened for by any U.S. state?

These questions and more can help you better understand the evidence development behind newborn screening and what is needed to add conditions to state panels.

For more than 50 years, every newborn in the U.S. has been screened for a range of debilitating and deadly diseases through a simple heel prick. Each year, 12,000 babies and their families benefit from early detection and life saving treatments made possible by newborn screening.

The Newborn Screening Resource Roadmap is designed to help anyone new to newborn screening navigate key topics and resources so that you can advocate effectively for newborn screening in your state.

🔗 Learn more and check out our new Roadmap here: https://everylifefoundation.org/newborn-screening-take-action/newborn-screening-resource-roadmap/

01/26/2026

We are looking forward to WORLDSymposium 2026, where the global lysosomal disease community comes together to share science, insights, and progress.

NS Pharma is proud to be presenting at this year’s meeting, contributing to important conversations focused on advancing research and care for individuals living with rare genetic conditions.

We value the opportunity to engage with clinicians, researchers, and advocates who are dedicated to improving outcomes across the rare disease landscape.

If you haven't already, register here: https://ow.ly/xVLP50Y3CtS

01/21/2026

We’re proud to support ongoing clinical research to improve the lives of people living with Duchenne muscular dystrophy (DMD).

Among the trials we sponsor is Brogidirsen (NS-089/NCNP-02), which recently presented 3.5-year efficacy and safety data at the 2025 World Muscle Society Congress.

If you or someone you care for is interested in learning more or participating in a DMD clinical trial, visit our clinical trials page for details and eligibility information:
https://ow.ly/tq9s50Y0xOy

01/14/2026

We are happy to be heading to Miami, FL for the upcoming CureDuchenne Workshop! 💙

This gathering offers a welcoming space for families, caregivers, clinicians, and researchers to come together and explore the latest insights in Duchenne muscular dystrophy. It is a great chance to learn, ask questions, and connect with others who share the same hope for progress.

📅 Date: Saturday, January 17, 2026
🕗 Time: 8:00 AM to 4:00 PM
📍 Location: Miami Marriott Dadeland, 9090 S Dadeland Blvd, Miami, FL 33156

Register and learn more: https://ow.ly/K9wp50XWBs7

We look forward to seeing everyone there and taking part in a day of learning and connection.!