11/13/2025
FDA Clears Gene Therapy Trial for GA.
The FDA has approved the initiation of the Opti-GAIN phase 1/2 clinical trial for CTx001, an adeno-associated virus (AAV)-based gene therapy targeting geographic atrophy (GA) secondary to age-related macular degeneration (AMD). Developed by Complement Therapeutics, CTx001 delivers a truncated versio...