PTC Therapeutics

PTC Therapeutics Contact information, map and directions, contact form, opening hours, services, ratings, photos, videos and announcements from PTC Therapeutics, Pharmaceutical Company, 500 Warren Corporate Center Drive, Warren, NJ.

PTC is a patient-centered biopharmaceutical company focused on discovering, developing & commercializing medicine for children and adults living with rare disease.

As we reflect on Rare Disease Day, we recognize the strength of the rare disease community—patients, families, caregiver...
03/06/2026

As we reflect on Rare Disease Day, we recognize the strength of the rare disease community—patients, families, caregivers, advocates, clinicians, and researchers—who inspire progress every day.

A commitment to rare diseases is at the heart of who we are. We’re proud to stand with the community and to work with purpose to advance research and support for people living with rare conditions.

To everyone impacted by a rare disease: we see you, we support you, and we’re with you.

At the upcoming 2026 American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting next week...
03/05/2026

At the upcoming 2026 American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting next week, PTC is excited to share the latest insights on our research and data around advancing care for the treatment of phenylketonuria with healthcare professionals and the broader PKU community. We’re committed to advancing science, strengthening collaboration, and keeping the needs of the PKU community at the center of everything we do. If you’re attending, we invite you to connect with us—stop by our booth ( #1523) to learn more, meet our teams, and exchange insights that will shape the future of clinical genetics.

🌟 We’re thrilled to announce that PTC has been honored with the 2026 Gallup Exceptional Workplace Award—our 5th time! 🎉 ...
03/04/2026

🌟 We’re thrilled to announce that PTC has been honored with the 2026 Gallup Exceptional Workplace Award—our 5th time! 🎉 A huge thank you to our incredible teams who embody our culture every day.

At PTC, we embrace our strengths through Gallup CliftonStrengths, fostering individual growth and enhancing collaboration within our global community. 💪✨

We appreciate our dedicated employees for their unwavering commitment to our mission and the patients and families we serve.

Learn more: https://www.ptcbio.com/posts/ptc-earns-gallups-exceptional-workplace-award-for-fifth-year

02/28/2026

🌍✨ On this Rare Disease Day, we honor the millions of individuals living with a rare condition around the globe. At PTC, we believe that true progress begins with listening.

This day serves as a reminder of the importance of understanding the realities faced by those impacted by rare diseases. Their experiences shape our commitment to support and create meaningful change.

Join us as we reflect on what it truly means to stand by the rare disease community. Together, we can amplify their voices and ensure that their needs are at the forefront of our mission.

Let’s listen with purpose and act with commitment.

Learn more: https://ow.ly/Uxa550YliqQ

02/23/2026

PKU is rare—but the strength of the PKU community is extraordinary. For many individuals and families, living with PKU means thoughtful planning around food, regular monitoring of Phe levels, and navigating the day-to-day emotions that can come with managing a lifelong condition.

As we approach Rare Disease Day on February 28, we’re proud to amplify voices from the global community—including people living with the condition, healthcare professionals, and advocacy leaders—sharing what life is really like and why awareness and support make such a meaningful difference.

Watch, listen, and share to help us elevate PKU voices. Hear more of their stories here: https://ow.ly/3mHO50YkmRV

02/16/2026

We’re proud to stand with the global rare disease community—and to reinforce our commitment to individuals and families impacted by AADC deficiency ( ).

Because for ultra-rare conditions like AADCd, the journey to answers can be long. As pediatric neurologist Dr. Marcus Wheeler shares, symptoms can overlap with other metabolic disorders, meaning specialists often need to cast a broad diagnostic net—and awareness can be a barrier.

We’re working to help change that through education, advocacy, and support for the AADC deficiency community—so more patients can be recognized sooner and connected to appropriate care.

Hear more from Dr. Wheeler: https://ow.ly/X72850YevT1

When Luke Millington joined PTC's Talent Pipeline Program, he was seeking valuable experience at a global biopharmaceuti...
02/09/2026

When Luke Millington joined PTC's Talent Pipeline Program, he was seeking valuable experience at a global biopharmaceutical company. Instead, he found a profound opportunity to support individuals living with Duchenne muscular dystrophy ( ), a condition PTC has passionately advocated for through years of research and innovation.

As a member of our Patient Advocacy team, Luke leverages his lived experience to assist families in navigating the critical transition from childhood to adult DMD care. His journey exemplifies our commitment to empowering patients and healthcare professionals alike, ensuring that every voice is heard and every need is addressed.

Join us in uplifting the rare community all month long by learning more about Luke’s inspiring story. Together, we can make a meaningful difference in the lives of those affected by rare diseases.

Read more about Luke’s journey here: https://ow.ly/sAUi50YavHN

02/02/2026

At PTC Therapeutics, our commitment to those with significant unmet medical needs pushes us every day. In recognition of this month, we're sharing stories from a few of the brave individuals living with a rare disorder. Meet Tiffany, a courageous mother of two living with Friedreich's ataxia ( ), a rare neuromuscular disorder impacting the central nervous system and heart. Tiffany's journey highlights the power of community and the hope that comes from connecting with others facing similar challenges. 💪❤️ Join us in celebrating her resilience and learn more about her inspiring story: https://ow.ly/FpMH50Y6nzU

Pam and Kelsey are helping to raise awareness of phenylketonuria (PKU) by sharing their inspiring story. Read more in th...
01/28/2026

Pam and Kelsey are helping to raise awareness of phenylketonuria (PKU) by sharing their inspiring story. Read more in the link below.

Pam Kowalczyk struggles with the genetic condition PKU, which prevents the body from processing protein. Years ago, she decided to adopt a child with the same condition. Now they manage it together.

12/03/2025

Today, on PKU Awareness Day, we're honored to share Tracy's story.

Tracy is an astrophysicist and NASA contractor who has lived with classical PKU her entire life. Managing a strict low-protein diet, staying balanced while traveling, and navigating school and career demands have shaped her health journey, resilience, and discipline.

Learn more about how PKU has influenced Tracy's life and why advocacy continues to matter: https://bit.ly/4pQ8vND

11/22/2025

When Sarah Chamberlin's daughter was diagnosed with phenylketonuria (PKU), she channeled her experience into creating meaningful change for others living with this rare condition. Today, as the Founder & Executive Director of flok, Sarah continues to advance support and research for the inherited metabolic disorder community. Learn more about her journey: https://bit.ly/48e2i6P

10/23/2025

Aromatic L-amino acid decarboxylase (AADC) deficiency is a rare condition with complex physical and emotional challenges. This AADC Deficiency Awareness Day, we stand with families navigating AADC deficiency and honor their resilience and commitment to overcoming the challenges of this rare condition that is often misdiagnosed. For young Simone and his family, testing at a local hospital didn’t reveal the cause of his symptoms. It was only after traveling to a specialist children's hospital in Italy that they finally received the diagnosis that would change their journey.

Learn more about Simone's path to diagnosis and how has impacted his family: https://bit.ly/43nCt2w

Address

500 Warren Corporate Center Drive
Warren, NJ
07059

Opening Hours

Monday 9am - 5pm
Tuesday 9am - 5pm
Wednesday 9am - 5pm
Thursday 9am - 5pm
Friday 9am - 5pm

Telephone

+19082227000

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Our Story

Everyone has a different definition of progress. For the last 20 years, we’ve measured our progress researching rare disease in moments. Smiling ones and crying ones. Moments spent with our patients’ families and ones with their friends. We know that every step forward comes after several steps backward, because we’ve lived it—whether spending time with families in their homes or with our scientists researching in our labs in central New Jersey.

It can be easy to lose yourself as you progress further. Although we’ve grown, our heart remains in the same place, because we’ve never measured ourselves like larger companies do. Our biggest accomplishment has always been the time we can give to all of our families. Whether it’s hours, days, months, or years, every small moment is a big win.

COMMUNITY GUIDELINES

Thank you for your interest in PTC Therapeutics. We’re happy you’re here! This Page is a place for community members to engage with us, learn about our corporate initiatives and programs, and participate in an open dialogue with other members of the PTC and rare disease communities.