American Society of Gene & Cell Therapy

11/26/2025

ASGCT is pleased to see two CGT products recognized with the Commissioner’s National Priority Voucher (CNVP). We continue to advocate for safe and effective regulatory frameworks. Read a summary of our recent comment letters on other FDA initiatives:

ASGCT recently submitted three comment letters to the US Food and Drug Administration (FDA) focused on advancing regulatory flexibility and modernization…

11/25/2025

Your voice matters! We proudly offer FREE membership to patients and caregivers of individuals living with rare diseases, and significantly discounted membership to advocates in our new Allied Member category.

Join ASGCT today! 📧 Find out if you qualify: membership@asgct.org

11/24/2025

We want to see your research! Submit your abstract for the opportunity to present at , May 11-15 in Boston, MA.

11/24/2025

Master CGT fundamentals in our new FREE online course! Learn the essentials – from CRISPR to clinical trial design and more – on your own schedule.

🆕The latest topics + trends in our rapidly expanding field
🧠 Developed by leading experts in cell + gene therapy
💻 Free, self-paced, and interactive

Visit the ASGCT Learning Center to enroll today: https://learning.asgct.org/auth/imis?origin=%2Fasgct

11/21/2025

Thanks to all who kicked off Breakthroughs in Targeted In Vivo Gene Editing with us today – what an incredible day of cutting-edge science and insights in this exciting field!

11/20/2025

As cell and gene therapies revolutionize modern medicine, South America is emerging as a dynamic player on the global stage. Join this FREE webinar exploring South American technological frontiers:

As cell and gene therapies revolutionize modern medicine, South America is emerging as a dynamic player on the global stage—leveraging scientific…

11/19/2025

"Our moment is now. It's now that we have the very first tools to start asking, what happens if we deliver gene therapy to the whole brain? Can we get this done?"

Hear Dr. Sonia Vallabh's powerful personal journey to develop a treatment for prion disease in our latest Community Quick Take: https://patienteducation.asgct.org/research-clinical-trials/community-quick-takes/patient-journey-gene-editing-for-prion-disease

11/19/2025

Secure your livestream access and unlock one year of on-demand recordings! 🔓 Don't miss out on this must-attend gene editing event: asgct.org/breakthroughs

11/18/2025

Recent news reports highlighting commercial efforts to normalize heritable human genome editing (HHGE) underscore the urgent need for sustained vigilance, ethical clarity, and enforceable global governance.

Claims that germline editing should proceed because “the technology is ready” disregard the absence of both the demonstration of technical feasibility without adverse effects and the absence of legitimate clinical necessity. Such ventures risk undermining public trust in the entire field of genetic medicine, conflating speculative enhancement with legitimate, life-saving somatic gene therapies.

Read more:

Recent news reports highlighting commercial efforts to normalize heritable human genome editing (HHGE) underscore the urgent need for sustained vigilance,…

11/17/2025

Can't travel to San Diego? Join our targeted gene editing event via livestream and get one year of on-demand access! 📱 Register: asgct.org/breakthroughs

11/16/2025

November is National Epilepsy Awareness Month! ASGCT is honored to go with this large and resilient community, especially the advocates, organizations, and researchers working toward treatments.

💜 Epilepsy can impact anyone, regardless of age, race, or gender.
💜 Not all seizures are the same, and many people experience more than one type.
💜 Misunderstanding and misinformation about seizures contribute to stigma.

With nearly 1,000 identified genes that can play a role, research is advancing cell and gene therapy approaches for specific genetic forms of epilepsy. Learn more about how gene therapy and viral vectors work at patienteducation.asgct.org.

11/13/2025

It's ! 💙 Genetic counselors are essential partners in helping individuals and families understand how genetics can impact their health. They play many roles, one being guiding patients and families through genetic testing. Through genetic testing, counselors can help identify whether a condition has a genetic cause, develop plans to manage or treat it, and provide guidance on whether it could be passed on to future generations.

Learn more in this Community Quick Take:

Genetic testing plays a critical role in deciding whether a person can participate in a clinical trial. Learn from our experts highlighting the unique…